Amish, Mennonite, and Hutterite
Genetic Disorder Database

Renpenning syndrome

Disorder
OMIM #: #309500  (Click to access OMIM database)
Disorder: Renpenning syndrome 
Also known as: X-linked mental retardation 
Clinical
Phenotype: males affected: microcephaly, facial dysmorphism, difficultiy feeding, short stature, lean build, small testes, scoliosis, sparse hair, muscle atrophy, cleft palate, congenital heart defect, developmental delay,  
Seen In: Amish
Old Order Mennonite
Old Colony Mennonite
Unknown/Other Mennonite
Hutterite
Remarks: X-linked recessive 
Mutations
1   Unknown / Other Mennonite  
Gene: PQBP1
Base Change: c.640dupC
Amino Acid Change: p.Arg214Profs*13
Last updated: 2023-02-02 

References
Lenski C, Abidi F, Meindl A, Gibson A, Platzer M, Kooy R, Lubs H, Stevenson R, Ramser J, Schwartz C. (2004) Novel Truncating Mutations in the Polyglutamine Tract binding Protein 1 Gene (PQBP1) Cause Renpenning Syndrome and X-Linked Mental Retardation in Another Family with Microcephaly. Am J Hum Genet Apr;74(4):777-80.
PubMed ID: 15024694 
Renpenning HJ, Gerrard JW, Zaleski WA, Tabata T. (1962) Familial sex-linked mental retardation. Can Med Assoc J Nov 3;87(18):954-6.
PubMed ID: 13981686 
Stevenson RE, Arena JF, Ouzts E, Gibson A, Shokeir MH, Vnencak-Jones C, Lubs HA, May M, Schwartz CE. (1998) Renpenning syndrome maps to Xp11. Am J Hum Genet May;62(5):1092-101.
PubMed ID: 9545405 

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