Amish, Mennonite, and Hutterite
Genetic Disorder Database

Hypomyelinating leukodystrophy 2

Disorder
OMIM #: #608804  (Click to access OMIM database)
Disorder: Hypomyelinating leukodystrophy 2 
Also known as: PELIZAEUS-MERZBACHER-LIKE DISEASE, 1
PMLD1 
Clinical
Phenotype: leukodystrophy, motor delay, poor head/trunk control, head titration, hypotonia, ataxia, spasticity, rigidity, choreoathetosis, developmental delay, cerebral atrophy, demyelination, optic atrophy 
Seen In: Amish
Old Order Mennonite
Old Colony Mennonite
Unknown/Other Mennonite
Hutterite
Remarks: Autosomal recessive 
Mutations
1   Amish  
Gene: GJC2
Base Change: A>G, at nucleotide 203
Amino Acid Change: tyr 68 --> cys
Last updated: 2023-01-03 

References
Crowgey EL, Washburn MC, Kolb EA, Puffenberger EG. (2019) Development of a Novel Next-Generation Sequencing Assay for Carrier Screening in Old Order Amish and Mennonite Populations of Pennsylvania. J Mol Diagn Jul;21(4):687-694.
PubMed ID: 31028937 

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