Amish, Mennonite, and Hutterite
Genetic Disorder Database

Amish infantile epilepsy syndrome

Disorder
OMIM #: #609056  (Click to access OMIM database)
Disorder: Amish infantile epilepsy syndrome 
Also known as: EPILEPSY SYNDROME, INFANTILE-ONSET SYMPTOMATIC, GM3 SYNTHASE DEFICIENCY 
Clinical
Phenotype: infantile-onset seizures, irritability, feeding difficulties, failure to thrive, vomiting, developmental delay/mental retardation, blindness 
Seen In: Amish
Old Order Mennonite
Old Colony Mennonite
Unknown/Other Mennonite
Hutterite
Remarks:  
Mutations
1   Amish  
Gene: SIAT9, E8 region
Base Change: C>T, at nucleotide 694
Amino Acid Change: arg 232 --> term
Last updated: 2009-03-15 

References
Simpson MA, Cross H, Proukakis C, Priestman DA, Neville DC, Reinkensmeier G, Wang H, Wiznitzer M, Gurtz K, Verganelaki A, Pryde A, Patton MA, Dwek RA, Butters TD, Platt FM, and Crosby AH. (2004) Infantile-onset symptomatic epilepsy syndrome caused by a homozygous loss-of-function mutation of GM3 synthase. Nat Genet 36(11): 1225-1229.
PubMed ID: 15502825 

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